Researchers have worked out the exact function of an enzyme that is critical for normal muscle structure and is involved in several muscular dystrophies. The findings could be used to develop rapid, ...
A novel potential therapy based on a natural human protein significantly slows muscle damage and improves function in mice who have the same genetic mutation as boys with the most common form of ...
Duchenne muscular dystrophy - a rare, genetic, neuromuscular disease that primarily affects males - leads to degeneration and weakness of muscles. The heart, being a muscle, is not spared by this ...
Please provide your email address to receive an email when new articles are posted on . Viltepso, an injection treatment for Duchenne muscular dystrophy in patients with a confirmed mutation, ...
Please provide your email address to receive an email when new articles are posted on . Interim results also showed reduction of the neurodegenerative biomarker neurofilament light chain. Serious ...
The least-squares mean difference in the Hammersmith Functional Motor Scale-Expanded change from baseline at 12 months was 1.8 points for those 2 to 12 years receiving apitegromab vs placebo.
Treatment Market is projected to grow at a healthy rate of around 13% by 2026. This growth is primarily driven by the increasing prevalence of SMA, growing awareness of early diagnosis and treatment, ...
Muscle tissue provides the largest store of potentially available protein in the body; it is considerable reduced in children with severe protein energy malnutrition (PEM). After nutritional recovery ...
Some patients with later-onset spinal muscular atrophy (SMA) type 2 and type 3 had improved motor function when the investigational monoclonal antibody apitegromab was added to their treatment, the ...
Aims: Benefits of resistance exercise in elderly people are well documented; however, sustaining these benefits can be difficult and adherence is often poor. Muscular strength and physical function ...