In a preclinical study, researchers applied an innovative treatment approach for genetic hearing loss and found that it ...

Scientists from the Gray Faculty of Medical & Health Sciences at Tel Aviv University introduced an innovative gene therapy ...

A new analyst survey suggests that doctors are still prescribing Sarepta’s Elevidys, even after a series of deaths in certain ...

Jesse Gelsinger died after receiving a gene therapy treatment to treat a liver disease. The death sparked an investigation ...

Capsida is investigating the root cause of the death, which occurred in the first patient treated in a trial of the company’s ...

As AAV9 and CRISPR programs navigate safety, delivery and scalability hurdles, small molecules offer a deployable, scalable ...

And it has paved the way for other therapeutic strategies, including the first gene therapy delivered through skin grafts, ...

The Food and Drug Administration (FDA) has approved updated labeling for Vyjuvek ® (beremagene geperpavec-svdt), a topical gene therapy for the treatment of wounds in adult and pediatric patients with ...

VintaBio™, a technology-forward company, announced today that it has filed provisional patents with the US Patent Office ...

The first participant in an investigational gene therapy trial of STXBP1 encephalopathy died, Capsida Biotherapeutics said.